Golodirsen restores DMD transcript imbalance in Duchenne Muscular Dystrophy patient muscle cells.

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Bibliographic Details
Title: Golodirsen restores DMD transcript imbalance in Duchenne Muscular Dystrophy patient muscle cells.
Authors: Rossi, Rachele1,2 (AUTHOR), Torelli, Silvia1,2 (AUTHOR), Moore, Marc1,2,3 (AUTHOR), Ala, Pierpaolo1,2 (AUTHOR), Morgan, Jennifer1,2 (AUTHOR), Malhotra, Jyoti4 (AUTHOR), Muntoni, Francesco1,2 (AUTHOR) f.muntoni@ucl.ac.uk
Source: Skeletal Muscle. 11/29/2024, Vol. 14 Issue 1, p1-14. 14p.
Database: Academic Search Ultimate
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