Methodological insights from the EPISTOP trial to designing clinical trials in rare diseases—A secondary analysis of a randomized clinical trial.

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Title: Methodological insights from the EPISTOP trial to designing clinical trials in rare diseases—A secondary analysis of a randomized clinical trial.
Authors: Wied, Stephanie1 (AUTHOR) swied@ukaachen.de, Hilgers, Ralf-Dieter1 (AUTHOR), Heussen, Nicole1,2 (AUTHOR), Kotulska, Katarzyna3 (AUTHOR), Dirani, Maya4 (AUTHOR), Kuchenbuch, Mathieu4 (AUTHOR), Jozwiak, Sergiusz5 (AUTHOR), Nabbout, Rima4 (AUTHOR)
Source: PLoS ONE. 12/3/2024, Vol. 19 Issue 12, p1-14. 14p.
Database: Academic Search Ultimate
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ISSN:19326203
DOI:10.1371/journal.pone.0312936