Enhanced fetal hemoglobin production via dual-beneficial mutation editing of the HBG promoter in hematopoietic stem and progenitor cells for β-hemoglobinopathies.

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Title: Enhanced fetal hemoglobin production via dual-beneficial mutation editing of the HBG promoter in hematopoietic stem and progenitor cells for β-hemoglobinopathies.
Authors: Chandraprabha, Prathibha Babu1,2 (AUTHOR), Azhagiri, Manoj Kumar K.1,2 (AUTHOR), Venkatesan, Vigneshwaran1,2 (AUTHOR), Magis, Wendy3 (AUTHOR), Prasad, Kirti1,2 (AUTHOR), Suresh, Sevanthy1,2 (AUTHOR), Pai, Aswin Anand4 (AUTHOR), Marepally, Srujan1 (AUTHOR), Srivastava, Alok1,4 (AUTHOR), Mohankumar, Kumarasamypet Murugesan1 (AUTHOR), Martin, David I. K.3 (AUTHOR), Thangavel, Saravanabhavan1 (AUTHOR) sthangavel@cmcvellore.ac.in
Source: Stem Cell Research & Therapy. 12/31/2024, Vol. 15 Issue 1, p1-19. 19p.
Database: Academic Search Ultimate
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ISSN:17576512
DOI:10.1186/s13287-024-04117-0