Long-term neuropsychologic outcome of pre-emptive mTOR inhibitor treatment in children with tuberous sclerosis complex (TSC) under 4 months of age (PROTECT), a two-arm, randomized, observer-blind, controlled phase IIb national multicentre clinical trial: study protocol
Saved in:
| Title: | Long-term neuropsychologic outcome of pre-emptive mTOR inhibitor treatment in children with tuberous sclerosis complex (TSC) under 4 months of age (PROTECT), a two-arm, randomized, observer-blind, controlled phase IIb national multicentre clinical trial: study protocol |
|---|---|
| Authors: | Driedger, Jan H.1 (AUTHOR), Schröter, Julian1 (AUTHOR), Hertzberg, Christoph (AUTHOR), Weschke, Bernhard (AUTHOR), Kaindl, Angela M. (AUTHOR), Lücke, Thomas (AUTHOR), Thiels, Charlotte (AUTHOR), Klotz, Kerstin Alexandra (AUTHOR), Fazeli, Walid (AUTHOR), Rostásy, Kevin (AUTHOR), Wiethoff-Ubrig, Lucia (AUTHOR), Kaiser, Olaf (AUTHOR), Trollmann, Regina (AUTHOR), Mammadova, Dilbar (AUTHOR), Schubert-Bast, Susanne (AUTHOR), Bach, Alexia (AUTHOR), Eckenweiler, Matthias (AUTHOR), Schönberger, Jan (AUTHOR), Martakis, Kyriakos (AUTHOR), Hahn, Andreas (AUTHOR) |
| Source: | Orphanet Journal of Rare Diseases. 1/6/2025, Vol. 20, p1-10. 10p. |
| Database: | Academic Search Ultimate |
|
Full text is not displayed to guests.
Login for full access.
|
|
| ISSN: | 17501172 |
|---|---|
| DOI: | 10.1186/s13023-024-03495-1 |
