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Long-term neuropsychologic outcome of pre-emptive mTOR inhibitor treatment in children with tuberous sclerosis complex (TSC) under 4 months of age (PROTECT), a two-arm, randomized, observer-blind, controlled phase IIb national multicentre clinical trial: study protocol

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Title: Long-term neuropsychologic outcome of pre-emptive mTOR inhibitor treatment in children with tuberous sclerosis complex (TSC) under 4 months of age (PROTECT), a two-arm, randomized, observer-blind, controlled phase IIb national multicentre clinical trial: study protocol
Authors: Driedger, Jan H.1 (AUTHOR), Schröter, Julian1 (AUTHOR), Hertzberg, Christoph (AUTHOR), Weschke, Bernhard (AUTHOR), Kaindl, Angela M. (AUTHOR), Lücke, Thomas (AUTHOR), Thiels, Charlotte (AUTHOR), Klotz, Kerstin Alexandra (AUTHOR), Fazeli, Walid (AUTHOR), Rostásy, Kevin (AUTHOR), Wiethoff-Ubrig, Lucia (AUTHOR), Kaiser, Olaf (AUTHOR), Trollmann, Regina (AUTHOR), Mammadova, Dilbar (AUTHOR), Schubert-Bast, Susanne (AUTHOR), Bach, Alexia (AUTHOR), Eckenweiler, Matthias (AUTHOR), Schönberger, Jan (AUTHOR), Martakis, Kyriakos (AUTHOR), Hahn, Andreas (AUTHOR)
Source: Orphanet Journal of Rare Diseases. 1/6/2025, Vol. 20, p1-10. 10p.
Database: Academic Search Ultimate
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  Data: Long-term neuropsychologic outcome of pre-emptive mTOR inhibitor treatment in children with tuberous sclerosis complex (TSC) under 4 months of age (PROTECT), a two-arm, randomized, observer-blind, controlled phase IIb national multicentre clinical trial: study protocol
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  Data: <searchLink fieldCode="JN" term="%22Orphanet+Journal+of+Rare+Diseases%22">Orphanet Journal of Rare Diseases</searchLink>. 1/6/2025, Vol. 20, p1-10. 10p.
PLink https://search.ebscohost.com/login.aspx?direct=true&site=eds-live&db=asn&AN=182324116
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