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Long-term outcomes of imiglucerase treatment in children with Gaucher disease type 1 or type 3 starting therapy before the age of 2 years.

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Bibliographic Details
Title: Long-term outcomes of imiglucerase treatment in children with Gaucher disease type 1 or type 3 starting therapy before the age of 2 years.
Authors: Mistry, Pramod K.1 (AUTHOR), Carwile, Jenny L.2 (AUTHOR), Burrow, Andrew3 (AUTHOR), Ganesh, Jaya4 (AUTHOR), Camelo, José Simon5 (AUTHOR), Hennermann, Julia B.6 (AUTHOR), Batista, Julie L.2 (AUTHOR), Oliveira-dos-Santos, Antonio7 (AUTHOR), Perichon, Maria G.2 (AUTHOR), Tantawy, Azza8 (AUTHOR)
Source: Molecular Genetics & Metabolism. Feb2025, Vol. 144 Issue 2, pN.PAG-N.PAG. 1p.
Database: Academic Search Ultimate
Description
ISSN:10967192
DOI:10.1016/j.ymgme.2024.108858