Seizures and movement disorders in patients with CLN2 disease treated with cerliponase alfa in the real-world setting.

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Bibliographic Details
Title: Seizures and movement disorders in patients with CLN2 disease treated with cerliponase alfa in the real-world setting.
Authors: Schulz, Angela1 (AUTHOR), Nickel, Miriam1 (AUTHOR), Schwering, Christoph1 (AUTHOR), Wibbeler, Eva1 (AUTHOR), Westermann, Lena Marie1 (AUTHOR), Hagenah, Luca1 (AUTHOR), Reddy, Sheila2 (AUTHOR), Hunt, Abigail2 (AUTHOR), Hunger, Matthias3 (AUTHOR), Okoli, Olivia4 (AUTHOR), Reisewitz, Pascal2 (AUTHOR)
Source: Molecular Genetics & Metabolism. Feb2025, Vol. 144 Issue 2, pN.PAG-N.PAG. 1p.
Database: Academic Search Ultimate
Description
ISSN:10967192
DOI:10.1016/j.ymgme.2024.108932