Health outcomes and drug utilisation in children with Noonan syndrome: a European cohort study.
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| Title: | Health outcomes and drug utilisation in children with Noonan syndrome: a European cohort study. |
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| Authors: | Santoro, Michele1 (AUTHOR) michele.santoro@cnr.it, Barisic, Ingeborg2 (AUTHOR), Coi, Alessio1 (AUTHOR), Tan, Joachim3,4 (AUTHOR), Garne, Ester5 (AUTHOR), Loane, Maria6 (AUTHOR), Odak, Ljubica7 (AUTHOR), Abate, Maria Valentina1 (AUTHOR), Ballardini, Elisa8 (AUTHOR), Cavero-Carbonell, Clara9 (AUTHOR), Gatt, Miriam10 (AUTHOR), Gissler, Mika11,12,13 (AUTHOR), Klungsøyr, Kari14,15 (AUTHOR), Lelong, Nathalie16 (AUTHOR), Tucker, David17 (AUTHOR), Wellesley, Diana18 (AUTHOR), Morris, Joan K.4 (AUTHOR) |
| Source: | Orphanet Journal of Rare Diseases. 2/17/2025, Vol. 20 Issue 1, p1-9. 9p. |
| Database: | Academic Search Ultimate |
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| ISSN: | 17501172 |
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| DOI: | 10.1186/s13023-025-03594-7 |