Clinical and economic burden of achondroplasia in the United States: results from a retrospective, observational study.

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Bibliographic Details
Title: Clinical and economic burden of achondroplasia in the United States: results from a retrospective, observational study.
Authors: Merchant, Nadia1 (AUTHOR), Alvir, Jose2 (AUTHOR), Ericksen, Paulette Negron2 (AUTHOR) Paulette.M.Ericksen@pfizer.com, Loftus, Jane3 (AUTHOR), Cara, Jose Francisco2 (AUTHOR), Slade, Alison4 (AUTHOR), Wajnrajch, Michael P.2,5 (AUTHOR), Baker, Christine L.2 (AUTHOR)
Source: Orphanet Journal of Rare Diseases. 2/27/2025, Vol. 20 Issue 1, p1-10. 10p.
Database: Academic Search Ultimate
Description
ISSN:17501172
DOI:10.1186/s13023-024-03268-w