First-in-human clinical study of an embryonic stem cell product for urea cycle disorders.

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Bibliographic Details
Title: First-in-human clinical study of an embryonic stem cell product for urea cycle disorders.
Authors: Umezawa, Akihiro1,2 (AUTHOR) umezawa-a@ncchd.go.jp, Fukuda, Akinari3 (AUTHOR), Horikawa, Reiko3 (AUTHOR), Uchida, Hajime3 (AUTHOR), Enosawa, Shin1 (AUTHOR), Oishi, Yoshie3 (AUTHOR), Nakamura, Naoko1 (AUTHOR), Sasaki, Kengo3,4 (AUTHOR), Yanagi, Yusuke3 (AUTHOR), Shimizu, Seiichi3 (AUTHOR), Nakao, Toshimasa3 (AUTHOR), Kodama, Tasuku3 (AUTHOR), Sakamoto, Seisuke3 (AUTHOR), Hayakawa, Itaru3 (AUTHOR), Akiyama, Saeko1,2 (AUTHOR), Saku, Noriaki1 (AUTHOR), Miyata, Shoko1 (AUTHOR), Ite, Kenta1 (AUTHOR), Javaregowda, Palaksha Kanive1,5 (AUTHOR), Toyoda, Masashi1 (AUTHOR)
Source: Stem Cell Research & Therapy. 3/6/2025, Vol. 16 Issue 1, p1-11. 11p.
Database: Academic Search Ultimate
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ISSN:17576512
DOI:10.1186/s13287-025-04162-3