Safety and efficacy of long term asfotase alfa treatment in childhood hypophosphatasia.

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Title: Safety and efficacy of long term asfotase alfa treatment in childhood hypophosphatasia.
Authors: d'Angelo, Debora Mariarita1 (AUTHOR), Lauriola, Federico1 (AUTHOR), Silvestrini, Luisa1 (AUTHOR), Cinque, Luigia2 (AUTHOR), Castori, Marco2 (AUTHOR), Di Donato, Giulia1 (AUTHOR), Di Ludovico, Armando1 (AUTHOR), La Bella, Saverio1 (AUTHOR), Chiarelli, Francesco1 (AUTHOR), Giannini, Cosimo1 (AUTHOR) cosimo.giannini@unich.it, Breda, Luciana1 (AUTHOR)
Source: Italian Journal of Pediatrics. 3/20/2025, Vol. 51 Issue 1, p1-6. 6p.
Database: Academic Search Ultimate
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ISSN:17208424
DOI:10.1186/s13052-025-01883-2