Muscle‐specific gene editing improves molecular and phenotypic defects in a mouse model of myotonic dystrophy type 1.
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| Title: | Muscle‐specific gene editing improves molecular and phenotypic defects in a mouse model of myotonic dystrophy type 1. |
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| Authors: | Izzo, Mariapaola1,2 (AUTHOR), Battistini, Jonathan1 (AUTHOR), Golini, Elisabetta1,3 (AUTHOR), Voellenkle, Christine4 (AUTHOR), Provenzano, Claudia1 (AUTHOR), Orsini, Tiziana1,3 (AUTHOR), Strimpakos, Georgios1 (AUTHOR), Scavizzi, Ferdinando1,3 (AUTHOR), Raspa, Marcello1,3 (AUTHOR), Baci, Denisa4 (AUTHOR), Frolova, Svetlana4 (AUTHOR), Tastsoglou, Spyros4 (AUTHOR), Zaccagnini, Germana4 (AUTHOR), Garcia‐Manteiga, Jose Manuel5 (AUTHOR), Gourdon, Genevieve6 (AUTHOR), Mandillo, Silvia1,3 (AUTHOR), Cardinali, Beatrice1 (AUTHOR) beatrice.cardinali@cnr.it, Martelli, Fabio4 (AUTHOR) Fabio.Martelli@grupposandonato.it, Falcone, Germana1 (AUTHOR) germana.falcone@cnr.it |
| Source: | Clinical & Translational Medicine. Feb2025, Vol. 15 Issue 2, p1-28. 28p. |
| Database: | Academic Search Ultimate |
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| ISSN: | 20011326 |
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| DOI: | 10.1002/ctm2.70227 |