Muscle‐specific gene editing improves molecular and phenotypic defects in a mouse model of myotonic dystrophy type 1.

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Title: Muscle‐specific gene editing improves molecular and phenotypic defects in a mouse model of myotonic dystrophy type 1.
Authors: Izzo, Mariapaola1,2 (AUTHOR), Battistini, Jonathan1 (AUTHOR), Golini, Elisabetta1,3 (AUTHOR), Voellenkle, Christine4 (AUTHOR), Provenzano, Claudia1 (AUTHOR), Orsini, Tiziana1,3 (AUTHOR), Strimpakos, Georgios1 (AUTHOR), Scavizzi, Ferdinando1,3 (AUTHOR), Raspa, Marcello1,3 (AUTHOR), Baci, Denisa4 (AUTHOR), Frolova, Svetlana4 (AUTHOR), Tastsoglou, Spyros4 (AUTHOR), Zaccagnini, Germana4 (AUTHOR), Garcia‐Manteiga, Jose Manuel5 (AUTHOR), Gourdon, Genevieve6 (AUTHOR), Mandillo, Silvia1,3 (AUTHOR), Cardinali, Beatrice1 (AUTHOR) beatrice.cardinali@cnr.it, Martelli, Fabio4 (AUTHOR) Fabio.Martelli@grupposandonato.it, Falcone, Germana1 (AUTHOR) germana.falcone@cnr.it
Source: Clinical & Translational Medicine. Feb2025, Vol. 15 Issue 2, p1-28. 28p.
Database: Academic Search Ultimate
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  Data: Muscle‐specific gene editing improves molecular and phenotypic defects in a mouse model of myotonic dystrophy type 1.
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  Data: <searchLink fieldCode="JN" term="%22Clinical+%26+Translational+Medicine%22">Clinical & Translational Medicine</searchLink>. Feb2025, Vol. 15 Issue 2, p1-28. 28p.
PLink https://search.ebscohost.com/login.aspx?direct=true&site=eds-live&db=asn&AN=184046583
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        Value: 10.1002/ctm2.70227
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        Text: English
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              Text: Feb2025
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              Y: 2025
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