Muscle‐specific gene editing improves molecular and phenotypic defects in a mouse model of myotonic dystrophy type 1.
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| Title: | Muscle‐specific gene editing improves molecular and phenotypic defects in a mouse model of myotonic dystrophy type 1. |
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| Authors: | Izzo, Mariapaola1,2 (AUTHOR), Battistini, Jonathan1 (AUTHOR), Golini, Elisabetta1,3 (AUTHOR), Voellenkle, Christine4 (AUTHOR), Provenzano, Claudia1 (AUTHOR), Orsini, Tiziana1,3 (AUTHOR), Strimpakos, Georgios1 (AUTHOR), Scavizzi, Ferdinando1,3 (AUTHOR), Raspa, Marcello1,3 (AUTHOR), Baci, Denisa4 (AUTHOR), Frolova, Svetlana4 (AUTHOR), Tastsoglou, Spyros4 (AUTHOR), Zaccagnini, Germana4 (AUTHOR), Garcia‐Manteiga, Jose Manuel5 (AUTHOR), Gourdon, Genevieve6 (AUTHOR), Mandillo, Silvia1,3 (AUTHOR), Cardinali, Beatrice1 (AUTHOR) beatrice.cardinali@cnr.it, Martelli, Fabio4 (AUTHOR) Fabio.Martelli@grupposandonato.it, Falcone, Germana1 (AUTHOR) germana.falcone@cnr.it |
| Source: | Clinical & Translational Medicine. Feb2025, Vol. 15 Issue 2, p1-28. 28p. |
| Database: | Academic Search Ultimate |
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| Header | DbId: asn DbLabel: Academic Search Ultimate An: 184046583 AccessLevel: 2 PubType: Academic Journal PubTypeId: academicJournal PreciseRelevancyScore: 0 |
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| PLink | https://search.ebscohost.com/login.aspx?direct=true&site=eds-live&db=asn&AN=184046583 |
| RecordInfo | BibRecord: BibEntity: Identifiers: – Type: doi Value: 10.1002/ctm2.70227 Languages: – Code: eng Text: English PhysicalDescription: Pagination: PageCount: 28 StartPage: 1 Titles: – TitleFull: Muscle‐specific gene editing improves molecular and phenotypic defects in a mouse model of myotonic dystrophy type 1. Type: main BibRelationships: HasContributorRelationships: – PersonEntity: Name: NameFull: Izzo, Mariapaola – PersonEntity: Name: NameFull: Battistini, Jonathan – PersonEntity: Name: NameFull: Golini, Elisabetta – PersonEntity: Name: NameFull: Voellenkle, Christine – PersonEntity: Name: NameFull: Provenzano, Claudia – PersonEntity: Name: NameFull: Orsini, Tiziana – PersonEntity: Name: NameFull: Strimpakos, Georgios – PersonEntity: Name: NameFull: Scavizzi, Ferdinando – PersonEntity: Name: NameFull: Raspa, Marcello – PersonEntity: Name: NameFull: Baci, Denisa – PersonEntity: Name: NameFull: Frolova, Svetlana – PersonEntity: Name: NameFull: Tastsoglou, Spyros – PersonEntity: Name: NameFull: Zaccagnini, Germana – PersonEntity: Name: NameFull: Garcia‐Manteiga, Jose Manuel – PersonEntity: Name: NameFull: Gourdon, Genevieve – PersonEntity: Name: NameFull: Mandillo, Silvia – PersonEntity: Name: NameFull: Cardinali, Beatrice – PersonEntity: Name: NameFull: Martelli, Fabio – PersonEntity: Name: NameFull: Falcone, Germana IsPartOfRelationships: – BibEntity: Dates: – D: 01 M: 02 Text: Feb2025 Type: published Y: 2025 Identifiers: – Type: issn-print Value: 20011326 Numbering: – Type: volume Value: 15 – Type: issue Value: 2 Titles: – TitleFull: Clinical & Translational Medicine Type: main |
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