Unlocking the Mysteries of Rare Disease Drug Development: A Beginner's Guide for Clinical Pharmacologists.
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| Title: | Unlocking the Mysteries of Rare Disease Drug Development: A Beginner's Guide for Clinical Pharmacologists. |
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| Authors: | Ahmed, Mariam A.1 (AUTHOR) mariam.ahmed@takeda.com, AbuAsal, Bilal2 (AUTHOR), Barrett, Jeffrey S.3 (AUTHOR), Azer, Karim4 (AUTHOR), Hon, Yuen Yi5 (AUTHOR), Albusaysi, Salwa6 (AUTHOR), Shang, Elizabeth7 (AUTHOR), Wang, Meng5 (AUTHOR), Burian, Maria8 (AUTHOR), Rayad, Noha9 (AUTHOR) |
| Source: | CTS: Clinical & Translational Science. Apr2025, Vol. 18 Issue 4, p1-21. 21p. |
| Database: | Academic Search Ultimate |
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| ISSN: | 17528054 |
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| DOI: | 10.1111/cts.70215 |