Economic burden of propionic acidemia in the United States: a claims-based study.
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| Title: | Economic burden of propionic acidemia in the United States: a claims-based study. |
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| Authors: | Perera, Sue1 (AUTHOR), Banerjee, Geetanjoli1 (AUTHOR), Cook, Erin E.2 (AUTHOR), Mu, Fan2 (AUTHOR), Cheng, Mu2 (AUTHOR), Zhang, Adina2 (AUTHOR), Lan, Jessie Jie2 (AUTHOR), Zou, Lin2 (AUTHOR), Sikirica, Vanja3 (AUTHOR) Vanja.Sikirica@modernatx.com |
| Source: | Orphanet Journal of Rare Diseases. 6/11/2025, Vol. 20 Issue 1, p1-12. 12p. |
| Database: | Academic Search Ultimate |
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| ISSN: | 17501172 |
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| DOI: | 10.1186/s13023-025-03836-8 |