Economic burden of propionic acidemia in the United States: a claims-based study.

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Bibliographic Details
Title: Economic burden of propionic acidemia in the United States: a claims-based study.
Authors: Perera, Sue1 (AUTHOR), Banerjee, Geetanjoli1 (AUTHOR), Cook, Erin E.2 (AUTHOR), Mu, Fan2 (AUTHOR), Cheng, Mu2 (AUTHOR), Zhang, Adina2 (AUTHOR), Lan, Jessie Jie2 (AUTHOR), Zou, Lin2 (AUTHOR), Sikirica, Vanja3 (AUTHOR) Vanja.Sikirica@modernatx.com
Source: Orphanet Journal of Rare Diseases. 6/11/2025, Vol. 20 Issue 1, p1-12. 12p.
Database: Academic Search Ultimate
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ISSN:17501172
DOI:10.1186/s13023-025-03836-8