Blueprint for clinical N-of-1 strategies with off-label precision treatments in monogenic epilepsies.
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| Title: | Blueprint for clinical N-of-1 strategies with off-label precision treatments in monogenic epilepsies. |
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| Authors: | Defelippe, Victoria M.1 (AUTHOR) V.M.Defelippe-2@umcutrecht.nl, Brilstra, Eva H.2 (AUTHOR), Otte, Willem M.1 (AUTHOR), van Thiel, Ghislaine J. M. W.3 (AUTHOR), Cross, Helen J.4 (AUTHOR), O'Callaghan, Finbar4 (AUTHOR), De Giorgis, Valentina5 (AUTHOR), Perucca, Emilio6,7 (AUTHOR), Braun, Kees P. J.1 (AUTHOR), Jansen, Floor E.1 (AUTHOR) |
| Source: | Orphanet Journal of Rare Diseases. 6/16/2025, Vol. 20 Issue 1, p1-17. 17p. |
| Database: | Academic Search Ultimate |
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| ISSN: | 17501172 |
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| DOI: | 10.1186/s13023-025-03750-z |