Assessment of physiological parameters in the application of a double adeno-associated virus 9 with a codon-optimized DYSF gene for limb girdle muscular dystrophy type R2.

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Bibliographic Details
Title: Assessment of physiological parameters in the application of a double adeno-associated virus 9 with a codon-optimized DYSF gene for limb girdle muscular dystrophy type R2.
Authors: Kuzubova, Elena V.1 kuzubova@bsuedu.ru, Radchenko, Alexandra I.1, Manuylov, Andrey A.2, Korokina, Ariana M.1, Koroleva, Natalia V.1, Yakovlev, Ivan A.3, Isaev, Arthur A.4, Deev, Roman V.5, Korokin, Mikhail V.1
Source: Research Results in Pharmacology. 2025, Vol. 11 Issue 2, p36-47. 12p.
Database: Academic Search Ultimate
Description
ISSN:2658381X
DOI:10.18413/rrpharmacology.11.642