A single amino acid variant in the variable region I of AAV capsid confers liver detargeting.

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Bibliographic Details
Title: A single amino acid variant in the variable region I of AAV capsid confers liver detargeting.
Authors: Xing, Ruxiao1 (AUTHOR), Xu, Mengyao1 (AUTHOR), Reil, Darcy1 (AUTHOR), Destefano, April1 (AUTHOR), Cui, Mengtian1 (AUTHOR), Liu, Nan1 (AUTHOR), Liang, Jialing1 (AUTHOR), Xu, Guangchao1 (AUTHOR), Luo, Li1 (AUTHOR), Xu, Meiyu1 (AUTHOR), Zhang, Fang1 (AUTHOR), Tai, Phillip W.L.1 (AUTHOR), Wei, Yuquan2 (AUTHOR), Gruntman, Alisha M.1 (AUTHOR), Flotte, Terence R.1 (AUTHOR), Gao, Guangping1,3 (AUTHOR) Guangping.Gao@umassmed.edu, Wang, Dan1,4 (AUTHOR) Dan.Wang@umassmed.edu
Source: PLoS Pathogens. 9/17/2025, Vol. 21 Issue 9, p1-16. 16p.
Database: Academic Search Ultimate
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ISSN:15537366
DOI:10.1371/journal.ppat.1013533