A single amino acid variant in the variable region I of AAV capsid confers liver detargeting.
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| Title: | A single amino acid variant in the variable region I of AAV capsid confers liver detargeting. |
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| Authors: | Xing, Ruxiao1 (AUTHOR), Xu, Mengyao1 (AUTHOR), Reil, Darcy1 (AUTHOR), Destefano, April1 (AUTHOR), Cui, Mengtian1 (AUTHOR), Liu, Nan1 (AUTHOR), Liang, Jialing1 (AUTHOR), Xu, Guangchao1 (AUTHOR), Luo, Li1 (AUTHOR), Xu, Meiyu1 (AUTHOR), Zhang, Fang1 (AUTHOR), Tai, Phillip W.L.1 (AUTHOR), Wei, Yuquan2 (AUTHOR), Gruntman, Alisha M.1 (AUTHOR), Flotte, Terence R.1 (AUTHOR), Gao, Guangping1,3 (AUTHOR) Guangping.Gao@umassmed.edu, Wang, Dan1,4 (AUTHOR) Dan.Wang@umassmed.edu |
| Source: | PLoS Pathogens. 9/17/2025, Vol. 21 Issue 9, p1-16. 16p. |
| Database: | Academic Search Ultimate |
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| ISSN: | 15537366 |
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| DOI: | 10.1371/journal.ppat.1013533 |