Clinically Important Endpoints in Individuals With Leukodystrophy: A Multisite Study.

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Bibliographic Details
Title: Clinically Important Endpoints in Individuals With Leukodystrophy: A Multisite Study.
Authors: Kotes, Emma R.1 (AUTHOR), Woidill, Sarah1 (AUTHOR), D'Aiello, Russell2 (AUTHOR), Khan, Amina2 (AUTHOR), McCann, Jacob3 (AUTHOR), Ramos, Mark2 (AUTHOR), Gavazzi, Francesco1 (AUTHOR), Keller, Stephanie4,5 (AUTHOR), Van Haren, Keith6,7 (AUTHOR), Fatemi, Ali8,9 (AUTHOR), Eichler, Florian10 (AUTHOR), Bonkowsky, Joshua11 (AUTHOR), Fraser, Jamie12 (AUTHOR), Emrick, Lisa13,14 (AUTHOR), Sherbini, Omar1 (AUTHOR), Hackett, Ashley4,5 (AUTHOR), Gauna, Jeilo7 (AUTHOR), Amos, Dandre15 (AUTHOR), Goodman, Jordan8 (AUTHOR), Fine, Amena Smith9 (AUTHOR)
Source: Annals of the Child Neurology Society. Sep2025, Vol. 3 Issue 3, p176-187. 12p.
Database: Academic Search Ultimate
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ISSN:28313267
DOI:10.1002/cns3.70025