Clinically Important Endpoints in Individuals With Leukodystrophy: A Multisite Study.

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Title: Clinically Important Endpoints in Individuals With Leukodystrophy: A Multisite Study.
Authors: Kotes, Emma R.1 (AUTHOR), Woidill, Sarah1 (AUTHOR), D'Aiello, Russell2 (AUTHOR), Khan, Amina2 (AUTHOR), McCann, Jacob3 (AUTHOR), Ramos, Mark2 (AUTHOR), Gavazzi, Francesco1 (AUTHOR), Keller, Stephanie4,5 (AUTHOR), Van Haren, Keith6,7 (AUTHOR), Fatemi, Ali8,9 (AUTHOR), Eichler, Florian10 (AUTHOR), Bonkowsky, Joshua11 (AUTHOR), Fraser, Jamie12 (AUTHOR), Emrick, Lisa13,14 (AUTHOR), Sherbini, Omar1 (AUTHOR), Hackett, Ashley4,5 (AUTHOR), Gauna, Jeilo7 (AUTHOR), Amos, Dandre15 (AUTHOR), Goodman, Jordan8 (AUTHOR), Fine, Amena Smith9 (AUTHOR)
Source: Annals of the Child Neurology Society. Sep2025, Vol. 3 Issue 3, p176-187. 12p.
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  Data: Clinically Important Endpoints in Individuals With Leukodystrophy: A Multisite Study.
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  Data: <searchLink fieldCode="JN" term="%22Annals+of+the+Child+Neurology+Society%22">Annals of the Child Neurology Society</searchLink>. Sep2025, Vol. 3 Issue 3, p176-187. 12p.
PLink https://search.ebscohost.com/login.aspx?direct=true&site=eds-live&db=asn&AN=188019283
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        Value: 10.1002/cns3.70025
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        Text: English
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      – TitleFull: Clinically Important Endpoints in Individuals With Leukodystrophy: A Multisite Study.
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              Text: Sep2025
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