Early Intervention and Speed-to-Effect in Spinal Muscular Atrophy Type 1 Following Onasemnogene Abeparvovec Gene Replacement Therapy: Results of aPost-Hoc Analysis of Pooled Clinical Study Data.
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| Title: | Early Intervention and Speed-to-Effect in Spinal Muscular Atrophy Type 1 Following Onasemnogene Abeparvovec Gene Replacement Therapy: Results of aPost-Hoc Analysis of Pooled Clinical Study Data. |
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| Authors: | Toro, Walter1 (AUTHOR) walter.toro_jimenez@novartis.com, Reyna, Sandra P.1 (AUTHOR), Ritter, Shannon1 (AUTHOR), Patel, Anish1 (AUTHOR), Mumneh, Nayla1 (AUTHOR), Dabbous, Omar1 (AUTHOR) |
| Source: | Neurology & Therapy. Oct2025, Vol. 14 Issue 5, p1903-1918. 16p. |
| Database: | Academic Search Ultimate |
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