Advances in gene therapy for Lafora disease: Intravenous recombinant adeno‐associated virus‐mediated delivery of EPM2A and EPM2B genes.
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| Title: | Advances in gene therapy for Lafora disease: Intravenous recombinant adeno‐associated virus‐mediated delivery of EPM2A and EPM2B genes. |
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| Authors: | Zafra‐Puerta, Luis1,2,3 (AUTHOR), Iglesias‐Cabeza, Nerea1 (AUTHOR), Sciaccaluga, Miriam3,4 (AUTHOR), Bellingacci, Laura5 (AUTHOR), Canonichesi, Jacopo5 (AUTHOR), Sánchez‐Martín, Gema1 (AUTHOR), Costa, Cinzia6 (AUTHOR), Sánchez, Marina P.1 (AUTHOR) msanchezg@fjd.es, Serratosa, José M.1 (AUTHOR) joseserratosa@me.com |
| Source: | Clinical & Translational Medicine. Nov2025, Vol. 15 Issue 11, p1-25. 25p. |
| Database: | Academic Search Ultimate |
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| ISSN: | 20011326 |
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| DOI: | 10.1002/ctm2.70514 |