Advances in gene therapy for Lafora disease: Intravenous recombinant adeno‐associated virus‐mediated delivery of EPM2A and EPM2B genes.

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Title: Advances in gene therapy for Lafora disease: Intravenous recombinant adeno‐associated virus‐mediated delivery of EPM2A and EPM2B genes.
Authors: Zafra‐Puerta, Luis1,2,3 (AUTHOR), Iglesias‐Cabeza, Nerea1 (AUTHOR), Sciaccaluga, Miriam3,4 (AUTHOR), Bellingacci, Laura5 (AUTHOR), Canonichesi, Jacopo5 (AUTHOR), Sánchez‐Martín, Gema1 (AUTHOR), Costa, Cinzia6 (AUTHOR), Sánchez, Marina P.1 (AUTHOR) msanchezg@fjd.es, Serratosa, José M.1 (AUTHOR) joseserratosa@me.com
Source: Clinical & Translational Medicine. Nov2025, Vol. 15 Issue 11, p1-25. 25p.
Database: Academic Search Ultimate
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ISSN:20011326
DOI:10.1002/ctm2.70514