LNP‐mediated in vivo base editing corrects Agxt to cure primary hyperoxaluria type 1.
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| Title: | LNP‐mediated in vivo base editing corrects Agxt to cure primary hyperoxaluria type 1. |
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| Authors: | Zhang, Dexin1 (AUTHOR), Zheng, Rui1 (AUTHOR), Chen, Zhoutong1 (AUTHOR), Chen, Xi2 (AUTHOR), Yang, Lei3 (AUTHOR), Huo, Yanan2 (AUTHOR), Zhao, Yining4 (AUTHOR), Huang, Jiaxin1 (AUTHOR), Zhang, Dan2 (AUTHOR), Yin, Shuming2 (AUTHOR), Li, Dali2,5 (AUTHOR) dlli@bio.ecnu.edu.cn, Geng, Hongquan1 (AUTHOR) genghongquan@fudan.edu.cn |
| Source: | Clinical & Translational Medicine. Nov2025, Vol. 15 Issue 11, p1-20. 20p. |
| Database: | Academic Search Ultimate |
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| ISSN: | 20011326 |
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| DOI: | 10.1002/ctm2.70533 |