LNP‐mediated in vivo base editing corrects Agxt to cure primary hyperoxaluria type 1.

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Bibliographic Details
Title: LNP‐mediated in vivo base editing corrects Agxt to cure primary hyperoxaluria type 1.
Authors: Zhang, Dexin1 (AUTHOR), Zheng, Rui1 (AUTHOR), Chen, Zhoutong1 (AUTHOR), Chen, Xi2 (AUTHOR), Yang, Lei3 (AUTHOR), Huo, Yanan2 (AUTHOR), Zhao, Yining4 (AUTHOR), Huang, Jiaxin1 (AUTHOR), Zhang, Dan2 (AUTHOR), Yin, Shuming2 (AUTHOR), Li, Dali2,5 (AUTHOR) dlli@bio.ecnu.edu.cn, Geng, Hongquan1 (AUTHOR) genghongquan@fudan.edu.cn
Source: Clinical & Translational Medicine. Nov2025, Vol. 15 Issue 11, p1-20. 20p.
Database: Academic Search Ultimate
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ISSN:20011326
DOI:10.1002/ctm2.70533