Base and Prime Editing for Inherited Retinal Diseases: Delivery Platforms, Safety, Efficacy, and Translational Perspectives.

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Title: Base and Prime Editing for Inherited Retinal Diseases: Delivery Platforms, Safety, Efficacy, and Translational Perspectives.
Authors: Zhang, Haoliang1,2 (AUTHOR), Li, Yuxuan2,3 (AUTHOR) liyuxuan608@sjtu.edu.cn, Li, Jiajie3 (AUTHOR), Li, Xiaosa1,2,4,5 (AUTHOR), Li, Tong1,2,4,5,6 (AUTHOR)
Source: Pharmaceutics. Nov2025, Vol. 17 Issue 11, p1405. 47p.
Database: Academic Search Ultimate
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ISSN:19994923
DOI:10.3390/pharmaceutics17111405