Towards effective cystic fibrosis gene therapy by optimizing prime editing and pulmonary-targeted LNPs.
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| Title: | Towards effective cystic fibrosis gene therapy by optimizing prime editing and pulmonary-targeted LNPs. |
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| Authors: | Lange, Kaya Sophie1,2 (AUTHOR), Wiesner, Lisa Marie1 (AUTHOR), Susat, Kathleen1 (AUTHOR), Köhler, Vera1 (AUTHOR), Lenger, Malte1 (AUTHOR), Michalek, Christian Alexander1 (AUTHOR), Baack, Anna-Lena1 (AUTHOR), Mundt, Philip Frederic1 (AUTHOR), Kanthak, Kai1 (AUTHOR), Guckes, Isabell Alexandra1 (AUTHOR), Sanfilippo, Liliana1 (AUTHOR), Haverkamp, Lucas1,2 (AUTHOR), Mahajan, Utkarsh Anil1,3 (AUTHOR), Zimmer, Felicitas Helena1,2 (AUTHOR), Zimmermann, Sinan1 (AUTHOR), Radukic, Marco Tobias2 (AUTHOR), Klages, Levin Joe4 (AUTHOR), Kalinowski, Jörn1,4 (AUTHOR), Müller, Kristian Mark1,2 (AUTHOR) Kristian@syntbio.net |
| Source: | Frontiers in Systems Biology. 2025, p1-14. 14p. |
| Database: | Academic Search Ultimate |
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| ISSN: | 26740702 |
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| DOI: | 10.3389/fsysb.2025.1603749 |