Towards effective cystic fibrosis gene therapy by optimizing prime editing and pulmonary-targeted LNPs.
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| Title: | Towards effective cystic fibrosis gene therapy by optimizing prime editing and pulmonary-targeted LNPs. |
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| Authors: | Lange, Kaya Sophie1,2 (AUTHOR), Wiesner, Lisa Marie1 (AUTHOR), Susat, Kathleen1 (AUTHOR), Köhler, Vera1 (AUTHOR), Lenger, Malte1 (AUTHOR), Michalek, Christian Alexander1 (AUTHOR), Baack, Anna-Lena1 (AUTHOR), Mundt, Philip Frederic1 (AUTHOR), Kanthak, Kai1 (AUTHOR), Guckes, Isabell Alexandra1 (AUTHOR), Sanfilippo, Liliana1 (AUTHOR), Haverkamp, Lucas1,2 (AUTHOR), Mahajan, Utkarsh Anil1,3 (AUTHOR), Zimmer, Felicitas Helena1,2 (AUTHOR), Zimmermann, Sinan1 (AUTHOR), Radukic, Marco Tobias2 (AUTHOR), Klages, Levin Joe4 (AUTHOR), Kalinowski, Jörn1,4 (AUTHOR), Müller, Kristian Mark1,2 (AUTHOR) Kristian@syntbio.net |
| Source: | Frontiers in Systems Biology. 2025, p1-14. 14p. |
| Database: | Academic Search Ultimate |
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| Header | DbId: asn DbLabel: Academic Search Ultimate An: 190299997 AccessLevel: 2 PubType: Academic Journal PubTypeId: academicJournal PreciseRelevancyScore: 0 |
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| PLink | https://search.ebscohost.com/login.aspx?direct=true&site=eds-live&db=asn&AN=190299997 |
| RecordInfo | BibRecord: BibEntity: Identifiers: – Type: doi Value: 10.3389/fsysb.2025.1603749 Languages: – Code: eng Text: English PhysicalDescription: Pagination: PageCount: 14 StartPage: 1 Titles: – TitleFull: Towards effective cystic fibrosis gene therapy by optimizing prime editing and pulmonary-targeted LNPs. Type: main BibRelationships: HasContributorRelationships: – PersonEntity: Name: NameFull: Lange, Kaya Sophie – PersonEntity: Name: NameFull: Wiesner, Lisa Marie – PersonEntity: Name: NameFull: Susat, Kathleen – PersonEntity: Name: NameFull: Köhler, Vera – PersonEntity: Name: NameFull: Lenger, Malte – PersonEntity: Name: NameFull: Michalek, Christian Alexander – PersonEntity: Name: NameFull: Baack, Anna-Lena – PersonEntity: Name: NameFull: Mundt, Philip Frederic – PersonEntity: Name: NameFull: Kanthak, Kai – PersonEntity: Name: NameFull: Guckes, Isabell Alexandra – PersonEntity: Name: NameFull: Sanfilippo, Liliana – PersonEntity: Name: NameFull: Haverkamp, Lucas – PersonEntity: Name: NameFull: Mahajan, Utkarsh Anil – PersonEntity: Name: NameFull: Zimmer, Felicitas Helena – PersonEntity: Name: NameFull: Zimmermann, Sinan – PersonEntity: Name: NameFull: Radukic, Marco Tobias – PersonEntity: Name: NameFull: Klages, Levin Joe – PersonEntity: Name: NameFull: Kalinowski, Jörn – PersonEntity: Name: NameFull: Müller, Kristian Mark IsPartOfRelationships: – BibEntity: Dates: – D: 17 M: 12 Text: 2025 Type: published Y: 2025 Identifiers: – Type: issn-print Value: 26740702 Titles: – TitleFull: Frontiers in Systems Biology Type: main |
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