Adeno-Associated Virus-Based Gene Therapy for Lafora Disease in Epm2b -Deficient Mice.

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Bibliographic Details
Title: Adeno-Associated Virus-Based Gene Therapy for Lafora Disease in Epm2b -Deficient Mice.
Authors: Zafra-Puerta, Luis1,2 (AUTHOR), Iglesias-Cabeza, Nerea1,2 (AUTHOR), Sanz, Pascual3,4 (AUTHOR), García-Gimeno, María Adelaida4,5 (AUTHOR), Sánchez-Martín, Gema1,5 (AUTHOR), Sánchez, Marina P.1 (AUTHOR), Serratosa, José M.1,2 (AUTHOR)
Source: International Journal of Molecular Sciences. Dec2025, Vol. 26 Issue 24, p11930. 18p.
Database: Academic Search Ultimate
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ISSN:16616596
DOI:10.3390/ijms262411930