GAMT Deficiency: Clinical Presentation, Treatment, Diagnosis, Animal Models, Preclinical and Clinical Developments.

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Bibliographic Details
Title: GAMT Deficiency: Clinical Presentation, Treatment, Diagnosis, Animal Models, Preclinical and Clinical Developments.
Authors: Biagiotti, Sara1 (AUTHOR), Perla, Elena1,2 (AUTHOR), Guzzo, Serafina Manila2,3 (AUTHOR), Tolve, Manuela3,4 (AUTHOR), Nardecchia, Francesca4,5 (AUTHOR), Rossi, Luigia1 (AUTHOR), Carducci, Claudia2,5 (AUTHOR), Pascucci, Tiziana2,3 (AUTHOR), Leuzzi, Vincenzo4 (AUTHOR), Magnani, Mauro1,5 (AUTHOR) mauro.magnani@uniurb.it
Source: International Journal of Molecular Sciences. Dec2025, Vol. 26 Issue 23, p11282. 23p.
Database: Academic Search Ultimate
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