An AAV-Based Therapy Approach for Neurological Phenotypes of X-Linked Adrenoleukodystrophy.

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Title: An AAV-Based Therapy Approach for Neurological Phenotypes of X-Linked Adrenoleukodystrophy.
Authors: Gornostal, Ekaterina1,2 (AUTHOR), Alsalloum, Almaqdad1,2 (AUTHOR), Degtyarev, Egor1,2,3 (AUTHOR), Kuznetsova, Ekaterina1,2,4 (AUTHOR), Levashova, Aygun1,2,5 (AUTHOR), Mishina, Daria1,2 (AUTHOR), Mingaleva, Natalia1,2 (AUTHOR), Mazloum, Ali1,2,3 (AUTHOR), Bogdanov, Viktor1,2,4 (AUTHOR), Krupinova, Julia1,2,3,5 (AUTHOR), Mikhalkov, Sergey2 (AUTHOR), Rybkina, Irina4 (AUTHOR), Mityaeva, Olga1,5 (AUTHOR), Volchkov, Pavel1,3,5 (AUTHOR) volchkov_py@academpharm.ru
Source: International Journal of Molecular Sciences. Dec2025, Vol. 26 Issue 23, p11645. 34p.
Database: Academic Search Ultimate
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ISSN:16616596
DOI:10.3390/ijms262311645