Barriers, Limitations, and Experiences with Clinical Trials—Treatment in Rare Diseases with Prader–Willi Syndrome as an Example.

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Title: Barriers, Limitations, and Experiences with Clinical Trials—Treatment in Rare Diseases with Prader–Willi Syndrome as an Example.
Authors: Butler, Merlin G.1 (AUTHOR) mbutler4@kumc.edu, Silvey, Spencer1 (AUTHOR), van Bosse, Harold J. P.1 (AUTHOR)
Source: Genes. Dec2025, Vol. 16 Issue 12, p1436. 19p.
Database: Academic Search Ultimate
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ISSN:20734425
DOI:10.3390/genes16121436