Barriers, Limitations, and Experiences with Clinical Trials—Treatment in Rare Diseases with Prader–Willi Syndrome as an Example.
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| Title: | Barriers, Limitations, and Experiences with Clinical Trials—Treatment in Rare Diseases with Prader–Willi Syndrome as an Example. |
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| Authors: | Butler, Merlin G.1 (AUTHOR) mbutler4@kumc.edu, Silvey, Spencer1 (AUTHOR), van Bosse, Harold J. P.1 (AUTHOR) |
| Source: | Genes. Dec2025, Vol. 16 Issue 12, p1436. 19p. |
| Database: | Academic Search Ultimate |
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| ISSN: | 20734425 |
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| DOI: | 10.3390/genes16121436 |