Eculizumab for Thrombotic Microangiopathy Induced by Onasemnogene Abeparvovec in Spinal Muscular Atrophy.

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Bibliographic Details
Title: Eculizumab for Thrombotic Microangiopathy Induced by Onasemnogene Abeparvovec in Spinal Muscular Atrophy.
Authors: Kersnik Levart, Tanja1 (AUTHOR), Olas Kar, Nina1 (AUTHOR), Močnik Pegan, Chiara2 (AUTHOR), Vrščaj, Eva2 (AUTHOR), Troha Gergeli, Anja2 (AUTHOR), Loboda, Tanja2 (AUTHOR), Osredkar, Damjan2,3 (AUTHOR)
Source: Case Reports in Nephrology & Dialysis. 2025, Vol. 15 Issue 1, p133-140. 8p.
Database: Academic Search Ultimate
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ISSN:22969705
DOI:10.1159/000546114