Improvements in quality of life outcomes among individuals with MPS IVA treated with elosulfase alfa: Results from the Morquio A Registry Study (MARS).
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| Title: | Improvements in quality of life outcomes among individuals with MPS IVA treated with elosulfase alfa: Results from the Morquio A Registry Study (MARS). |
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| Authors: | Campeau, Philippe M.1 (AUTHOR), Burton, Barbara K.2 (AUTHOR), Ellaway, Carolyn3 (AUTHOR), Guffon, Nathalie4 (AUTHOR), Hughes, Derralynn5 (AUTHOR), Hunt, Abigail6 (AUTHOR), Lail, Alice6 (AUTHOR), Lin, Hsiang-Yu7 (AUTHOR), Lin, Shuan Pei7 (AUTHOR), Magner, Martin8 (AUTHOR), Mitchell, John J.9 (AUTHOR), Reisewitz, Pascal6 (AUTHOR), Stepien, Karolina M.10 (AUTHOR) |
| Source: | Molecular Genetics & Metabolism. Feb2026, Vol. 147 Issue 2, pN.PAG-N.PAG. 1p. |
| Database: | Academic Search Ultimate |
| ISSN: | 10967192 |
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| DOI: | 10.1016/j.ymgme.2025.109352 |
