Effectiveness and Safety of Nusinersen and Risdiplam in Spinal Muscular Atrophy: A Systematic Review.
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| Title: | Effectiveness and Safety of Nusinersen and Risdiplam in Spinal Muscular Atrophy: A Systematic Review. |
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| Authors: | Mehrabian, Amin1 (AUTHOR), Auguste, Peter1 (AUTHOR), Grove, Amy1 (AUTHOR), Brown, Anna1 (AUTHOR), Parr, Janette1 (AUTHOR), Patel, Mubarak1 (AUTHOR), Butt, Furqan1 (AUTHOR), Donoghue, Jeremiah1 (AUTHOR), Yousefi, Mehdi1 (AUTHOR), Parsons, Jo1 (AUTHOR) j.e.parsons@bham.ac.uk |
| Source: | Annals of Clinical & Translational Neurology. Feb2026, Vol. 13 Issue 2, p218-241. 24p. |
| Database: | Academic Search Ultimate |
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| ISSN: | 23289503 |
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| DOI: | 10.1002/acn3.70274 |