AAV9‐DARS2 Gene Therapy Rescues Phenotype in Leukoencephalopathy with Brainstem and Spinal Cord Involvement and Lactate Elevation Patient Cells and Neuronal Dars2 Deficient Mice.
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| Title: | AAV9‐DARS2 Gene Therapy Rescues Phenotype in Leukoencephalopathy with Brainstem and Spinal Cord Involvement and Lactate Elevation Patient Cells and Neuronal Dars2 Deficient Mice. |
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| Authors: | Garofolo, I1 (AUTHOR), Lindsay, B1 (AUTHOR), Liang, Y2 (AUTHOR), Ratajczak, B1 (AUTHOR), Janowski, M2 (AUTHOR), Walczak, P2 (AUTHOR), Fatemi, A1,3 (AUTHOR), Nemeth, CL1,3 (AUTHOR) cmertz1@jh.edu |
| Source: | Annals of Neurology. Jan2026, Vol. 99 Issue 1, p59-72. 14p. |
| Database: | Academic Search Ultimate |
| ISSN: | 03645134 |
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| DOI: | 10.1002/ana.78037 |
