Learnings from Patient Mortality after Delandistrogene Moxeparvovec Administration: A Report of Two Cases and Expert Committee Considerations for Future Mitigation and Management.

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Title: Learnings from Patient Mortality after Delandistrogene Moxeparvovec Administration: A Report of Two Cases and Expert Committee Considerations for Future Mitigation and Management.
Authors: Shieh, Perry B.1 (AUTHOR), Proud, Crystal2 (AUTHOR), Diamond, Tamir3 (AUTHOR), Chapin, Catherine A.4 (AUTHOR), Ahmad, Jawad5 (AUTHOR), Salama, Alan D.6 (AUTHOR), Bönnemann, Carsten G.7 (AUTHOR), Soslow, Jonathan8 (AUTHOR), Byrne, Barry J.9 (AUTHOR), Veerapandiyan, Aravindhan10 (AUTHOR), Brandsema, John F.3 (AUTHOR), Matesanz, Susan3 (AUTHOR), Samelson-Jones, Benjamin J.3 (AUTHOR), Wilkins, Benjamin J.3 (AUTHOR), Gerber, Marianne11 (AUTHOR), Godwin Wild, Kara E.12 (AUTHOR), Mason, Stefanie12 (AUTHOR), Asher, Damon12 (AUTHOR), McDonald, Craig M.13 (AUTHOR), Mendell, Jerry R.12 (AUTHOR) JMendell@sarepta.com
Source: Human Gene Therapy. Mar2026, Vol. 37 Issue 5/6, p262-279. 18p.
Database: Academic Search Ultimate
Description
ISSN:10430342
DOI:10.1177/10430342261423168