Learnings from Patient Mortality after Delandistrogene Moxeparvovec Administration: A Report of Two Cases and Expert Committee Considerations for Future Mitigation and Management.
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| Title: | Learnings from Patient Mortality after Delandistrogene Moxeparvovec Administration: A Report of Two Cases and Expert Committee Considerations for Future Mitigation and Management. |
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| Authors: | Shieh, Perry B.1 (AUTHOR), Proud, Crystal2 (AUTHOR), Diamond, Tamir3 (AUTHOR), Chapin, Catherine A.4 (AUTHOR), Ahmad, Jawad5 (AUTHOR), Salama, Alan D.6 (AUTHOR), Bönnemann, Carsten G.7 (AUTHOR), Soslow, Jonathan8 (AUTHOR), Byrne, Barry J.9 (AUTHOR), Veerapandiyan, Aravindhan10 (AUTHOR), Brandsema, John F.3 (AUTHOR), Matesanz, Susan3 (AUTHOR), Samelson-Jones, Benjamin J.3 (AUTHOR), Wilkins, Benjamin J.3 (AUTHOR), Gerber, Marianne11 (AUTHOR), Godwin Wild, Kara E.12 (AUTHOR), Mason, Stefanie12 (AUTHOR), Asher, Damon12 (AUTHOR), McDonald, Craig M.13 (AUTHOR), Mendell, Jerry R.12 (AUTHOR) JMendell@sarepta.com |
| Source: | Human Gene Therapy. Mar2026, Vol. 37 Issue 5/6, p262-279. 18p. |
| Database: | Academic Search Ultimate |
| FullText | Text: Availability: 0 |
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| Header | DbId: asn DbLabel: Academic Search Ultimate An: 192230308 AccessLevel: 2 PubType: Academic Journal PubTypeId: academicJournal PreciseRelevancyScore: 0 |
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| PLink | https://search.ebscohost.com/login.aspx?direct=true&site=eds-live&db=asn&AN=192230308 |
| RecordInfo | BibRecord: BibEntity: Identifiers: – Type: doi Value: 10.1177/10430342261423168 Languages: – Code: eng Text: English PhysicalDescription: Pagination: PageCount: 18 StartPage: 262 Titles: – TitleFull: Learnings from Patient Mortality after Delandistrogene Moxeparvovec Administration: A Report of Two Cases and Expert Committee Considerations for Future Mitigation and Management. Type: main BibRelationships: HasContributorRelationships: – PersonEntity: Name: NameFull: Shieh, Perry B. – PersonEntity: Name: NameFull: Proud, Crystal – PersonEntity: Name: NameFull: Diamond, Tamir – PersonEntity: Name: NameFull: Chapin, Catherine A. – PersonEntity: Name: NameFull: Ahmad, Jawad – PersonEntity: Name: NameFull: Salama, Alan D. – PersonEntity: Name: NameFull: Bönnemann, Carsten G. – PersonEntity: Name: NameFull: Soslow, Jonathan – PersonEntity: Name: NameFull: Byrne, Barry J. – PersonEntity: Name: NameFull: Veerapandiyan, Aravindhan – PersonEntity: Name: NameFull: Brandsema, John F. – PersonEntity: Name: NameFull: Matesanz, Susan – PersonEntity: Name: NameFull: Samelson-Jones, Benjamin J. – PersonEntity: Name: NameFull: Wilkins, Benjamin J. – PersonEntity: Name: NameFull: Gerber, Marianne – PersonEntity: Name: NameFull: Godwin Wild, Kara E. – PersonEntity: Name: NameFull: Mason, Stefanie – PersonEntity: Name: NameFull: Asher, Damon – PersonEntity: Name: NameFull: McDonald, Craig M. – PersonEntity: Name: NameFull: Mendell, Jerry R. IsPartOfRelationships: – BibEntity: Dates: – D: 01 M: 03 Text: Mar2026 Type: published Y: 2026 Identifiers: – Type: issn-print Value: 10430342 Numbering: – Type: volume Value: 37 – Type: issue Value: 5/6 Titles: – TitleFull: Human Gene Therapy Type: main |
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