Liposomal CRISPR/Cas9-Mediated Local Genome Editing for Joint Disease in Mucopolysaccharidosis Type I.
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| Title: | Liposomal CRISPR/Cas9-Mediated Local Genome Editing for Joint Disease in Mucopolysaccharidosis Type I. |
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| Authors: | Santos, Hallana Souza1,2 (AUTHOR), Poletto, Edina1,2 (AUTHOR), Vera, Luisa Natalia Pimentel1,2,3 (AUTHOR), Farinon, Mirian3,4 (AUTHOR), Kubaski, Francyne2,5 (AUTHOR), Carneiro, Paola Barcelos1,2 (AUTHOR), Carniel, Willian da Silva2,4 (AUTHOR), Giugliani, Roberto2,3 (AUTHOR), Matte, Ursula1,2,4 (AUTHOR), Teixeira, Helder Ferreira4,5 (AUTHOR), Schuh, Roselena Silvestri1,4 (AUTHOR) roseschuh0@gmail.com, Baldo, Guilherme1,2,5 (AUTHOR) |
| Source: | Pharmaceutics. Mar2026, Vol. 18 Issue 3, p281. 16p. |
| Database: | Academic Search Ultimate |
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| ISSN: | 19994923 |
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| DOI: | 10.3390/pharmaceutics18030281 |