Short-Term Intensive Avalglucosidase Alfa Regimen in Late-Diagnosed Infantile Pompe Disease: A Case Report.
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| Title: | Short-Term Intensive Avalglucosidase Alfa Regimen in Late-Diagnosed Infantile Pompe Disease: A Case Report. |
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| Authors: | Gragnaniello, Vincenza1 (AUTHOR) vincenza.gragnaniello@aopd.veneto.it, Pozza, Alice2 (AUTHOR), Cazzorla, Chiara1 (AUTHOR), Gueraldi, Daniela1,2 (AUTHOR), Di Salvo, Giovanni2 (AUTHOR), Burlina, Alberto B.1 (AUTHOR) |
| Source: | Reports (MDPI AG). Mar2026, Vol. 9 Issue 1, p31. 10p. |
| Database: | Academic Search Ultimate |
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| ISSN: | 2571841X |
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| DOI: | 10.3390/reports9010031 |