Novel AAV843 Vector-Mediated Gene Replacement Therapy Rescues Primary Hyperoxaluria Type I in Mice.

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Bibliographic Details
Title: Novel AAV843 Vector-Mediated Gene Replacement Therapy Rescues Primary Hyperoxaluria Type I in Mice.
Authors: Zhang, Jingjia1,2 (AUTHOR), Yin, Ye1,2 (AUTHOR), Ji, Baowei1,2,3 (AUTHOR), Sun, Manqing1,2,4 (AUTHOR), Jiang, Yuanyan1,2,5 (AUTHOR), Wu, Xiaohui3,6 (AUTHOR), Xiao, Xiao1,4,5 (AUTHOR), Shen, Qian1,2,6 (AUTHOR), Wu, Xia3,5 (AUTHOR), Xu, Hong1,2,4,6 (AUTHOR)
Source: Cells (2073-4409). Apr2026, Vol. 15 Issue 7, p629. 20p.
Database: Academic Search Ultimate
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ISSN:20734409
DOI:10.3390/cells15070629