Novel AAV843 Vector-Mediated Gene Replacement Therapy Rescues Primary Hyperoxaluria Type I in Mice.
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| Title: | Novel AAV843 Vector-Mediated Gene Replacement Therapy Rescues Primary Hyperoxaluria Type I in Mice. |
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| Authors: | Zhang, Jingjia1,2 (AUTHOR), Yin, Ye1,2 (AUTHOR), Ji, Baowei1,2,3 (AUTHOR), Sun, Manqing1,2,4 (AUTHOR), Jiang, Yuanyan1,2,5 (AUTHOR), Wu, Xiaohui3,6 (AUTHOR), Xiao, Xiao1,4,5 (AUTHOR), Shen, Qian1,2,6 (AUTHOR), Wu, Xia3,5 (AUTHOR), Xu, Hong1,2,4,6 (AUTHOR) |
| Source: | Cells (2073-4409). Apr2026, Vol. 15 Issue 7, p629. 20p. |
| Database: | Academic Search Ultimate |
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| ISSN: | 20734409 |
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| DOI: | 10.3390/cells15070629 |