The Placebo Effect in Rare Disease Clinical Trials: Measurement, Impact, and Statistical Approaches for Patient‐as‐Own‐Control Designs.

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Title: The Placebo Effect in Rare Disease Clinical Trials: Measurement, Impact, and Statistical Approaches for Patient‐as‐Own‐Control Designs.
Authors: Summar, Marshall L.1,2 (AUTHOR) msummar@uncommoncures.com, Woodcock, Janet3 (AUTHOR)
Source: CTS: Clinical & Translational Science. May2026, Vol. 19 Issue 5, p1-18. 18p.
Database: Academic Search Ultimate
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  Data: <searchLink fieldCode="JN" term="%22CTS%3A+Clinical+%26+Translational+Science%22">CTS: Clinical & Translational Science</searchLink>. May2026, Vol. 19 Issue 5, p1-18. 18p.
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        Value: 10.1111/cts.70550
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        Text: English
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              Text: May2026
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              Y: 2026
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