The Placebo Effect in Rare Disease Clinical Trials: Measurement, Impact, and Statistical Approaches for Patient‐as‐Own‐Control Designs.
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| Title: | The Placebo Effect in Rare Disease Clinical Trials: Measurement, Impact, and Statistical Approaches for Patient‐as‐Own‐Control Designs. |
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| Authors: | Summar, Marshall L.1,2 (AUTHOR) msummar@uncommoncures.com, Woodcock, Janet3 (AUTHOR) |
| Source: | CTS: Clinical & Translational Science. May2026, Vol. 19 Issue 5, p1-18. 18p. |
| Database: | Academic Search Ultimate |
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| ISSN: | 17528054 |
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| DOI: | 10.1111/cts.70550 |