Pediatric pharmacokinetics and pharmacodynamics of guanabenz for the treatment of vanishing white matter.

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Title: Pediatric pharmacokinetics and pharmacodynamics of guanabenz for the treatment of vanishing white matter.
Authors: Franken, Linda G.1 (AUTHOR), van Lieshout, Bart1 (AUTHOR), Eugenio, Joshua1 (AUTHOR), Verbeek, Renate2 (AUTHOR), Voermans, Marije2,3 (AUTHOR), van den Berg, Elske2 (AUTHOR), Bet, Pierre1 (AUTHOR), Mathôt, Ron A. A.1 (AUTHOR), van der Laan, Dennis1 (AUTHOR), Abbink, Truus E. M.2 (AUTHOR), van der Knaap, Marjo S.2,3 (AUTHOR) ms.vanderknaap@amsterdamumc.nl, Bartelink, Imke H.1 (AUTHOR) i.bartelink@amsterdamumc.nl
Source: Scientific Reports. 6/19/2026, Vol. 16 Issue 1, p1-15. 15p.
Database: Academic Search Ultimate
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ISSN:20452322
DOI:10.1038/s41598-026-47959-9