Defining When Nusinersen Starts to Work: Time to Clinical Benefit in Patients with SMA Types 1–3 from a Real-World Cohort in China.

Saved in:
Bibliographic Details
Title: Defining When Nusinersen Starts to Work: Time to Clinical Benefit in Patients with SMA Types 1–3 from a Real-World Cohort in China.
Authors: Wu, Ying1 (AUTHOR), Li, Shuang1,2 (AUTHOR), Fan, Yanbin1 (AUTHOR), Wu, Yuan1,2 (AUTHOR), Zhang, Jie1 (AUTHOR), Dong, Hui1 (AUTHOR), Zhang, Yao1 (AUTHOR), Yang, Xiaoling1 (AUTHOR), Xiong, Hui1,2 (AUTHOR), Wei, Cuijie1 (AUTHOR)
Source: Diagnostics (2075-4418). Jun2026, Vol. 16 Issue 12, p1828. 13p.
Database: Academic Search Ultimate
Full text is not displayed to guests.
Description
ISSN:20754418
DOI:10.3390/diagnostics16121828