Defining When Nusinersen Starts to Work: Time to Clinical Benefit in Patients with SMA Types 1–3 from a Real-World Cohort in China.
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| Title: | Defining When Nusinersen Starts to Work: Time to Clinical Benefit in Patients with SMA Types 1–3 from a Real-World Cohort in China. |
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| Authors: | Wu, Ying1 (AUTHOR), Li, Shuang1,2 (AUTHOR), Fan, Yanbin1 (AUTHOR), Wu, Yuan1,2 (AUTHOR), Zhang, Jie1 (AUTHOR), Dong, Hui1 (AUTHOR), Zhang, Yao1 (AUTHOR), Yang, Xiaoling1 (AUTHOR), Xiong, Hui1,2 (AUTHOR), Wei, Cuijie1 (AUTHOR) |
| Source: | Diagnostics (2075-4418). Jun2026, Vol. 16 Issue 12, p1828. 13p. |
| Database: | Academic Search Ultimate |
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| ISSN: | 20754418 |
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| DOI: | 10.3390/diagnostics16121828 |