Systemic AAV-h GCDH Gene Therapy Alleviates Glutaric Acid Accumulation and Attenuates Chronic Brain Vacuolation in a Novel Mouse Model of Glutaric Aciduria Type I.
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| Title: | Systemic AAV-h GCDH Gene Therapy Alleviates Glutaric Acid Accumulation and Attenuates Chronic Brain Vacuolation in a Novel Mouse Model of Glutaric Aciduria Type I. |
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| Authors: | Kim, Su Jin1 (AUTHOR), Nam, Yu Hwa2 (AUTHOR), Joo, Eun Young1,3 (AUTHOR), Park, Jisun1 (AUTHOR), Park, Saeyoung2 (AUTHOR), Jung, Sung-Chul2,3 (AUTHOR) jungsc@ewha.ac.kr, Jin, Dong-Kyu3 (AUTHOR) jindk@skku.edu |
| Source: | International Journal of Molecular Sciences. Jun2026, Vol. 27 Issue 12, p5569. 13p. |
| Database: | Academic Search Ultimate |
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| ISSN: | 16616596 |
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| DOI: | 10.3390/ijms27125569 |
