Systemic AAV-h GCDH Gene Therapy Alleviates Glutaric Acid Accumulation and Attenuates Chronic Brain Vacuolation in a Novel Mouse Model of Glutaric Aciduria Type I.

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Title: Systemic AAV-h GCDH Gene Therapy Alleviates Glutaric Acid Accumulation and Attenuates Chronic Brain Vacuolation in a Novel Mouse Model of Glutaric Aciduria Type I.
Authors: Kim, Su Jin1 (AUTHOR), Nam, Yu Hwa2 (AUTHOR), Joo, Eun Young1,3 (AUTHOR), Park, Jisun1 (AUTHOR), Park, Saeyoung2 (AUTHOR), Jung, Sung-Chul2,3 (AUTHOR) jungsc@ewha.ac.kr, Jin, Dong-Kyu3 (AUTHOR) jindk@skku.edu
Source: International Journal of Molecular Sciences. Jun2026, Vol. 27 Issue 12, p5569. 13p.
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  Data: Systemic AAV-h GCDH Gene Therapy Alleviates Glutaric Acid Accumulation and Attenuates Chronic Brain Vacuolation in a Novel Mouse Model of Glutaric Aciduria Type I.
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  Data: <searchLink fieldCode="JN" term="%22International+Journal+of+Molecular+Sciences%22">International Journal of Molecular Sciences</searchLink>. Jun2026, Vol. 27 Issue 12, p5569. 13p.
PLink https://search.ebscohost.com/login.aspx?direct=true&site=eds-live&db=asn&AN=194911807
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        Value: 10.3390/ijms27125569
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      – Code: eng
        Text: English
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        PageCount: 13
        StartPage: 5569
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      – TitleFull: Systemic AAV-h GCDH Gene Therapy Alleviates Glutaric Acid Accumulation and Attenuates Chronic Brain Vacuolation in a Novel Mouse Model of Glutaric Aciduria Type I.
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            NameFull: Kim, Su Jin
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            NameFull: Nam, Yu Hwa
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            NameFull: Joo, Eun Young
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            NameFull: Park, Jisun
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            NameFull: Park, Saeyoung
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            NameFull: Jung, Sung-Chul
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              Text: Jun2026
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              Y: 2026
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