Systemic AAV-h GCDH Gene Therapy Alleviates Glutaric Acid Accumulation and Attenuates Chronic Brain Vacuolation in a Novel Mouse Model of Glutaric Aciduria Type I.
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| Title: | Systemic AAV-h GCDH Gene Therapy Alleviates Glutaric Acid Accumulation and Attenuates Chronic Brain Vacuolation in a Novel Mouse Model of Glutaric Aciduria Type I. |
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| Authors: | Kim, Su Jin1 (AUTHOR), Nam, Yu Hwa2 (AUTHOR), Joo, Eun Young1,3 (AUTHOR), Park, Jisun1 (AUTHOR), Park, Saeyoung2 (AUTHOR), Jung, Sung-Chul2,3 (AUTHOR) jungsc@ewha.ac.kr, Jin, Dong-Kyu3 (AUTHOR) jindk@skku.edu |
| Source: | International Journal of Molecular Sciences. Jun2026, Vol. 27 Issue 12, p5569. 13p. |
| Database: | Academic Search Ultimate |
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| FullText | Links: – Type: pdflink Text: Availability: 1 |
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| Header | DbId: asn DbLabel: Academic Search Ultimate An: 194911807 AccessLevel: 2 PubType: Academic Journal PubTypeId: academicJournal PreciseRelevancyScore: 0 |
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| Items | – Name: Title Label: Title Group: Ti Data: Systemic AAV-h GCDH Gene Therapy Alleviates Glutaric Acid Accumulation and Attenuates Chronic Brain Vacuolation in a Novel Mouse Model of Glutaric Aciduria Type I. – Name: Author Label: Authors Group: Au Data: <searchLink fieldCode="AR" term="%22Kim%2C+Su+Jin%22">Kim, Su Jin</searchLink><relatesTo>1</relatesTo> (AUTHOR)<br /><searchLink fieldCode="AR" term="%22Nam%2C+Yu+Hwa%22">Nam, Yu Hwa</searchLink><relatesTo>2</relatesTo> (AUTHOR)<br /><searchLink fieldCode="AR" term="%22Joo%2C+Eun+Young%22">Joo, Eun Young</searchLink><relatesTo>1,3</relatesTo> (AUTHOR)<br /><searchLink fieldCode="AR" term="%22Park%2C+Jisun%22">Park, Jisun</searchLink><relatesTo>1</relatesTo> (AUTHOR)<br /><searchLink fieldCode="AR" term="%22Park%2C+Saeyoung%22">Park, Saeyoung</searchLink><relatesTo>2</relatesTo> (AUTHOR)<br /><searchLink fieldCode="AR" term="%22Jung%2C+Sung-Chul%22">Jung, Sung-Chul</searchLink><relatesTo>2,3</relatesTo> (AUTHOR)<i> jungsc@ewha.ac.kr</i><br /><searchLink fieldCode="AR" term="%22Jin%2C+Dong-Kyu%22">Jin, Dong-Kyu</searchLink><relatesTo>3</relatesTo> (AUTHOR)<i> jindk@skku.edu</i> – Name: TitleSource Label: Source Group: Src Data: <searchLink fieldCode="JN" term="%22International+Journal+of+Molecular+Sciences%22">International Journal of Molecular Sciences</searchLink>. Jun2026, Vol. 27 Issue 12, p5569. 13p. |
| PLink | https://search.ebscohost.com/login.aspx?direct=true&site=eds-live&db=asn&AN=194911807 |
| RecordInfo | BibRecord: BibEntity: Identifiers: – Type: doi Value: 10.3390/ijms27125569 Languages: – Code: eng Text: English PhysicalDescription: Pagination: PageCount: 13 StartPage: 5569 Titles: – TitleFull: Systemic AAV-h GCDH Gene Therapy Alleviates Glutaric Acid Accumulation and Attenuates Chronic Brain Vacuolation in a Novel Mouse Model of Glutaric Aciduria Type I. Type: main BibRelationships: HasContributorRelationships: – PersonEntity: Name: NameFull: Kim, Su Jin – PersonEntity: Name: NameFull: Nam, Yu Hwa – PersonEntity: Name: NameFull: Joo, Eun Young – PersonEntity: Name: NameFull: Park, Jisun – PersonEntity: Name: NameFull: Park, Saeyoung – PersonEntity: Name: NameFull: Jung, Sung-Chul – PersonEntity: Name: NameFull: Jin, Dong-Kyu IsPartOfRelationships: – BibEntity: Dates: – D: 15 M: 06 Text: Jun2026 Type: published Y: 2026 Identifiers: – Type: issn-print Value: 16616596 Numbering: – Type: volume Value: 27 – Type: issue Value: 12 Titles: – TitleFull: International Journal of Molecular Sciences Type: main |
| ResultId | 1 |