Longitudinal Transcriptomic Analysis Reveals Systemic Effects of Risdiplam in Adults with Spinal Muscular Atrophy.

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Title: Longitudinal Transcriptomic Analysis Reveals Systemic Effects of Risdiplam in Adults with Spinal Muscular Atrophy.
Authors: Liguori, Maria1 (AUTHOR) maria.liguori@cnr.it, Consiglio, Arianna1,2 (AUTHOR), D'Errico, Eustachio2,3 (AUTHOR), Antonacci, Ylenia1,3,4 (AUTHOR), Coffa, Martina1 (AUTHOR), Introna, Alessandro2 (AUTHOR), Simone, Isabella Laura3,4 (AUTHOR)
Source: Brain Sciences (2076-3425). Jun2026, Vol. 16 Issue 6, p643. 14p.
Database: Academic Search Ultimate
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ISSN:20763425
DOI:10.3390/brainsci16060643