Longitudinal Transcriptomic Analysis Reveals Systemic Effects of Risdiplam in Adults with Spinal Muscular Atrophy.

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Title: Longitudinal Transcriptomic Analysis Reveals Systemic Effects of Risdiplam in Adults with Spinal Muscular Atrophy.
Authors: Liguori, Maria1 (AUTHOR) maria.liguori@cnr.it, Consiglio, Arianna1,2 (AUTHOR), D'Errico, Eustachio2,3 (AUTHOR), Antonacci, Ylenia1,3,4 (AUTHOR), Coffa, Martina1 (AUTHOR), Introna, Alessandro2 (AUTHOR), Simone, Isabella Laura3,4 (AUTHOR)
Source: Brain Sciences (2076-3425). Jun2026, Vol. 16 Issue 6, p643. 14p.
Database: Academic Search Ultimate
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  Data: Longitudinal Transcriptomic Analysis Reveals Systemic Effects of Risdiplam in Adults with Spinal Muscular Atrophy.
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  Data: <searchLink fieldCode="JN" term="%22Brain+Sciences+%282076-3425%29%22">Brain Sciences (2076-3425)</searchLink>. Jun2026, Vol. 16 Issue 6, p643. 14p.
PLink https://search.ebscohost.com/login.aspx?direct=true&site=eds-live&db=asn&AN=194912383
RecordInfo BibRecord:
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    Identifiers:
      – Type: doi
        Value: 10.3390/brainsci16060643
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      – Code: eng
        Text: English
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        PageCount: 14
        StartPage: 643
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      – TitleFull: Longitudinal Transcriptomic Analysis Reveals Systemic Effects of Risdiplam in Adults with Spinal Muscular Atrophy.
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            NameFull: Liguori, Maria
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            NameFull: Consiglio, Arianna
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            NameFull: D'Errico, Eustachio
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            NameFull: Antonacci, Ylenia
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            NameFull: Coffa, Martina
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            NameFull: Introna, Alessandro
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            NameFull: Simone, Isabella Laura
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            – D: 01
              M: 06
              Text: Jun2026
              Type: published
              Y: 2026
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