Longitudinal Transcriptomic Analysis Reveals Systemic Effects of Risdiplam in Adults with Spinal Muscular Atrophy.
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| Title: | Longitudinal Transcriptomic Analysis Reveals Systemic Effects of Risdiplam in Adults with Spinal Muscular Atrophy. |
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| Authors: | Liguori, Maria1 (AUTHOR) maria.liguori@cnr.it, Consiglio, Arianna1,2 (AUTHOR), D'Errico, Eustachio2,3 (AUTHOR), Antonacci, Ylenia1,3,4 (AUTHOR), Coffa, Martina1 (AUTHOR), Introna, Alessandro2 (AUTHOR), Simone, Isabella Laura3,4 (AUTHOR) |
| Source: | Brain Sciences (2076-3425). Jun2026, Vol. 16 Issue 6, p643. 14p. |
| Database: | Academic Search Ultimate |
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| FullText | Links: – Type: pdflink Text: Availability: 1 |
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| Header | DbId: asn DbLabel: Academic Search Ultimate An: 194912383 AccessLevel: 2 PubType: Academic Journal PubTypeId: academicJournal PreciseRelevancyScore: 0 |
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| PLink | https://search.ebscohost.com/login.aspx?direct=true&site=eds-live&db=asn&AN=194912383 |
| RecordInfo | BibRecord: BibEntity: Identifiers: – Type: doi Value: 10.3390/brainsci16060643 Languages: – Code: eng Text: English PhysicalDescription: Pagination: PageCount: 14 StartPage: 643 Titles: – TitleFull: Longitudinal Transcriptomic Analysis Reveals Systemic Effects of Risdiplam in Adults with Spinal Muscular Atrophy. Type: main BibRelationships: HasContributorRelationships: – PersonEntity: Name: NameFull: Liguori, Maria – PersonEntity: Name: NameFull: Consiglio, Arianna – PersonEntity: Name: NameFull: D'Errico, Eustachio – PersonEntity: Name: NameFull: Antonacci, Ylenia – PersonEntity: Name: NameFull: Coffa, Martina – PersonEntity: Name: NameFull: Introna, Alessandro – PersonEntity: Name: NameFull: Simone, Isabella Laura IsPartOfRelationships: – BibEntity: Dates: – D: 01 M: 06 Text: Jun2026 Type: published Y: 2026 Identifiers: – Type: issn-print Value: 20763425 Numbering: – Type: volume Value: 16 – Type: issue Value: 6 Titles: – TitleFull: Brain Sciences (2076-3425) Type: main |
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