A phase III double-blind, placebo-controlled, randomized withdrawal trial of 5‑aminolevulinic acid hydrochloride with sodium ferrous citrate for efficacy and safety in patients diagnosed as Leigh syndrome.

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Title: A phase III double-blind, placebo-controlled, randomized withdrawal trial of 5‑aminolevulinic acid hydrochloride with sodium ferrous citrate for efficacy and safety in patients diagnosed as Leigh syndrome.
Authors: Ohtake, Akira1,2 (AUTHOR), Abe, Yuichi1 (AUTHOR), Murayama, Kei3 (AUTHOR), Shiraishi, Hideaki4,5 (AUTHOR), Osaka, Hitoshi6 (AUTHOR), Kumada, Satoko7 (AUTHOR), Ito, Tetsuya8 (AUTHOR), Kondo, Hidehito9 (AUTHOR), Hamada, Yusuke10 (AUTHOR), Suzuki-Ajihara, Sayaka1,2 (AUTHOR), Arao, Masato1 (AUTHOR), Ueda, Yuki4 (AUTHOR), Nagai, Kohei6 (AUTHOR), Ichimoto, Keiko3 (AUTHOR), Matsunaga, Ayako3 (AUTHOR), Kashii, Hirofumi7 (AUTHOR), Nakajima, Yoko8 (AUTHOR), Nakagawa, Hitoshi11 (AUTHOR), Kurose, Shunichi11 (AUTHOR), Fukuda, Kaori11 (AUTHOR)
Source: PLoS ONE. 7/17/2026, Vol. 21 Issue 7, p1-22. 22p.
Database: Academic Search Ultimate
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